The teenager needs access to treatment that's only available in Europe and comes at a cost of £300,000. | ITV News Granada ...

About the FALCON Trial FALCON is a first-in-human, open-label, multi-center Phase 1b clinical trial designed to evaluate the safety and tolerability of SGT-212 in participants aged 18-40 who have been ...

Solid Biosciences Inc. (Nasdaq: SLDB) (the "Company” or "Solid”), a life sciences company developing precision genetic ...

Scientists reveal the GluD brain protein's active role, offering new hope for mental health. Discover how this breakthrough ...

Solid Biosciences Inc. (Nasdaq: SLDB) (the "Company" or "Solid"), a life sciences company developing precision genetic medicines for neuromuscular ...

SGT-212 has received FDA Fast Track, Rare Pediatric Disease and Orphan Drug designations - - Dosing of the first participant in the Phase 1b FALCON trial has been completed, with initial data expected ...

Learn more about the new study, which highlights the importance of analyzing brain structure and connectivity simultaneously.

IntraBio Inc. today announced positive topline results from its pivotal Phase III IB1001-303 clinical trial, "Effects of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T): A Randomized, ...

IntraBio Inc. today announced that the European Commission granted marketing authorization to AQNEURSA® (levacetylleucine) for the treatment of neurological manifestations of Niemann-Pick Type C (NPC) ...

A concert, six humanoid robots, and one flawless somersault. Together, they ignited not only the cheers of a crowd of more than 100,000 viewers, but also triggered a surge of wows in the cyberspace.

“I’ve always been curious about how the retinal cells in the eye survive for decades in such a harsh environment,” says Nicolas Bazan, neuroscientist at Louisiana State University (LSU) Health New ...

The glial-specific role of betaPix during cerebral blood vessel development has been revealed by establishing a new betaPix conditional trap allele in zebrafish.